Science Translational Medicine· Alvaro Murillo, Melanie Alpaugh, Ruban Rex Peter Durairaj, Emma L. Randall, Meghan Larin, Laura Heraty, Alys N. Aston, Alysha S. Taylor, Alex Mas Monteys, Nina Stöberl, Aeverie E. R. Heuchan, Pascale Aeschlimann, Kyle Fears, Christian Landles, Georgina F. Osborne, Antoine Mangin, Soumyasree Bhattacharyya, Emmanouil Metzakopian, Nicholas D. Allen, Jack Puymirat, Gillian P. Bates, Beverly L. Davidson, Francesca Cicchetti, Mariah J. Lelos, Vincent Dion·· 14 小时前AI 评分33
Cas9切口酶介导的CAG/CTG重复序列收缩与亨廷顿病小鼠模型的表型改善相关
Cas9 nickase–mediated contraction of CAG/CTG repeats is associated with phenotypic improvements in a Huntington’s disease mouse model
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Cas9切口酶介导的CAG/CTG重复序列收缩与亨廷顿病小鼠模型的表型改善相关。该研究发表于Science Translational Medicine，现有信息未提供样本量、具体表型指标或效应量。
来源：Science Translational Medicine · science.org