Science Translational Medicine· Jacob Helm, Elena Buena-Atienza, Clemens M. Sauter, Linus Wiora, Melanie Kraft, Yvonne Schelling, Jakob Admard, Jeannette Hübener-Schmid, Thomas Klockgether, Matthis Synofzik, Luís Pereira de Almeida, Mafalda Raposo, Paola Giunti, Hector Garcia-Moreno, Magda M. Santana, Jennifer Faber, Holger Hengel, Nicolas Casadei, Ludger Schöls, Stefan Hauser·· 14 小时前AI 评分21
单核苷酸多态性指导的脊髓小脑性共济失调3型等位基因特异性反义寡核苷酸设计
Single-nucleotide polymorphism–directed design of allele-specific antisense oligonucleotides for spinocerebellar ataxia type 3
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脊髓小脑性共济失调3型的等位基因特异性反义寡核苷酸设计以单核苷酸多态性为指导。该研究刊于Science Translational Medicine，所提供内容未披露实验设计、疗效或安全性结果。
来源：Science Translational Medicine · science.org